We are delighted to have a number of leading speakers from across the world as part of our programme.
Further details of the programme for each day can be found be clicking the date in question, alternatively you can look at the whole programme in PDF format using the link below.
Note that this version will change as the programme is finalized.
09:00 - 14:00 Conference registration desk open and poster setup
Conference opens 14:00
Introductory keynote presentation
Session one: Patient and industry forums
Drinks reception and poster viewing
Session two: Translational research in adult NMDs
Session three: Natural history, clinical outcome measures and standards of care in paediatric diseases
Poster session 1
Session four: Gene replacement: production and delivery of therapeutics
Session five: Emerging technologies and SOPs in diagnostics and biomarkers
Session six: Antisense technologies strategies and successes
Poster session 2
Session seven: Life quality versus quality of life
Session eight: Stem cell therapies towards clinical trials
Session nine: What is the future for translational research in rare diseases?
Closing keynote and final remarks
Conference closes 13:00